5-Year Data on Gleevec for 1st Line Patients on 400mg Dose

  •        Between 2000 and 2001, 1100 newly diagnosed patients were
    enrolled in the IRIS trials randomized into 2 arms, one taking
    Interferon/Ara-C and the other 400mg Gleevec.

  • The 5-year data has been published recently in the New England Journal
    of Medicine, November 2006.  The follow-up time is median 60 months.

  • Gleevec shows a definite superiority over Interferon/Ara-C in terms of
    responses, overall survivals and freedom from progression.  This is the
    reason Gleevec is now the first-line drug treatment.

  • The 12 months and 60 months complete cytogenetic response (CCR) rates
    were 69% and 87% respectively.  Only 7% of patients on Gleevec
    progressed into advanced phases in 5 years time.  The overall survival
    was 89% and when censored for transplant deaths and deaths unrelated to
    CML, the overall survival for newly diagnosed Gleevec patients on
    400mg is 95% at 5 years.  Due to the excellent response rates and 5-year
    survival data, Gleevec is now the first-line therapy treatment in CML
    even for young patients with suitable donors.  

  • In the IRIS trials, 65% of patients crossed over from the Interferon arm to
    join the Gleevec arm.  Only 4% of Gleevec patients discontinued
    treatment due to bad side-effects.  

  • The CHR rate at 5 years is 98%.

  • At the 12 month mark of Gleevec, 69% of patients reached a CCR and
    85% reached a major cytogenetic remission (MCR, 1-35%Ph+).  At the
    60 month mark of Gleevec, these numbers jumped to 87% CCR and 92%
    MCR proving that Gleevec responses can get deeper with time.

  • 96% of patients who are still receiving 400mg Gleevec from the trial had
    a CCR on Gleevec.

  • Responses followed the Sokal risk score with 89% of low-risk patients
    reaching CCR in 5 years followed by 82% of intermediate-risk patients
    and 69% of high-risk patients.  The risk of disease progression to
    advanced phases was also higher in high-risk patients at 17% in 5 years
    followed by 8% for intermediate-risk patients and 3% for low-risk
    patients.  However, those patients who were high-risk by the Sokal score
    but achieved a CCR, did not progress in disease.  A CCR with Gleevec
    gives the promise of long-term remissions for all patients whatever their
    risk score.

  • Regarding a major molecular response (MMR) which is defined as a
    1000-fold reduction of disease from diagnosis by PCR measurements, at
    12 months of Gleevec, 53% achieved this.  This number climbed to 80%
    in 4 years.  So, at 4 years of Gleevec, 80% of patients can achieve a
    MMR.

  • At the 5 year mark, 93% of newly diagnosed patients had not progressed
    in their disease.  The event-free survival (no relapses in chronic phase)
    was 83% at 5 years.

  • The rate of progression was 1.5% in the first year, 2.8% in the second
    year, 1.6% in the third year, 0.9% in the fourth year and 0.6% in the fifth
    year.  For patients in CCR, the rate of disease progression is 2.1% in the
    first year, 0.8% in the second year, 0.3% in the third year and no
    progression in the fourth year.  With a CCR on Gleevec, the longer you
    stay on the drug, less chances of disease progression as seen from the trial.

  • Out of 350 evaluable patients, of those who had a CCR at 12 months on
    Gleevec, 97% of them had not had disease progression.  93% of patients
    with a MCR had no disease progression at the 5 year mark.  However, of
    patients with no CCR, only 81% had no disease progression in 5 years.

  • Patients with a MMR to Gleevec at 18 months, there was 100%
    progression-free survival.  Patients with a CCR but less than a PCR 3-log
    reduction, there was 98% progression-free survival.  However, patients
    with no CCR, had a 87% progression-free survival at 5 years.

  • Gleevec with a 89% overall survival and a 17% relapse rate at 5 years
    with the relapse rate falling with time has become the first-line therapy
    option in CML.

  • For those patients who do not respond to Gleevec or who relapse from
    Gleevec, there are stronger drugs like Dasatinib, Nilotinib, Bosutinib and
    many others either FDA approved or in clinical trials.

    
Dr. Francois Guilhot's Summary of IRIS Trials